Safety and efficacy of mitapivat, an oral pyruvate kinase activator, in sickle cell disease: a phase 2, open-label study

Publication date

2022-07

Authors

van Dijk, Myrthe JORCID 0000-0002-9377-0367
Rab, M A E
van Oirschot, Birgitte AISNI 0000000391228600
Eijkelenboom-Bos, Jennifer
Derichs, Cleo
Rijneveld, Anita W
Cnossen, Marjon H
Nur, Erfan
Biemond, Bart J
Bartels, MarijeORCID 0000-0001-9685-1755

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taverne

Abstract

Keywords

Taverne, Hematology, Letter

Citation

van Dijk, M J, Rab, M A E, van Oirschot, B A, Bos, J, Derichs, C, Rijneveld, A W, Cnossen, M H, Nur, E, Biemond, B J, Bartels, M, Jans, J J M, van Solinge, W W, Schutgens, R E G, van Wijk, R & van Beers, E J 2022, 'Safety and efficacy of mitapivat, an oral pyruvate kinase activator, in sickle cell disease : a phase 2, open-label study', American Journal of Hematology, vol. 97, no. 7, pp. E226-E229. https://doi.org/10.1002/ajh.26554