Challenges and opportunities of adding CFTR modulators for cystic fibrosis to the WHO essential medicines list
Publication date
2025-09
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Abstract
Keywords
CFTR modulators, Cystic fibrosis, Elexacaftor/tezacaftor/ivacaftor, Equitable access, Essential medicines, Essential medicines list, Global Health, Medicines affordability, World health organization, Pediatrics, Perinatology, and Child Health, Pulmonary and Respiratory Medicine
Citation
Costa, E, van den Ham, H A & Leufkens, H G M 2025, 'Challenges and opportunities of adding CFTR modulators for cystic fibrosis to the WHO essential medicines list', Journal of Cystic Fibrosis, vol. 24, no. 5, pp. 920-922. https://doi.org/10.1016/j.jcf.2025.06.006