Challenges and opportunities of adding CFTR modulators for cystic fibrosis to the WHO essential medicines list

Publication date

2025-09

Authors

Costa, Enrico
van den Ham, H AORCID 0000-0003-1339-9818ISNI 0000000492480979
Leufkens, H.G.M.ISNI 0000000392454327

Editors

Advisors

Supervisors

Document Type

Article
Open Access logo

License

cc_by

Abstract

Keywords

CFTR modulators, Cystic fibrosis, Elexacaftor/tezacaftor/ivacaftor, Equitable access, Essential medicines, Essential medicines list, Global Health, Medicines affordability, World health organization, Pediatrics, Perinatology, and Child Health, Pulmonary and Respiratory Medicine

Citation

Costa, E, van den Ham, H A & Leufkens, H G M 2025, 'Challenges and opportunities of adding CFTR modulators for cystic fibrosis to the WHO essential medicines list', Journal of Cystic Fibrosis, vol. 24, no. 5, pp. 920-922. https://doi.org/10.1016/j.jcf.2025.06.006