Safety through design: Expanding options for spinal muscular atrophy gene therapy
Publication date
2025-09-11
Authors
Groen, Ewout J.N.
Wadman, Renske I
Editors
Advisors
Supervisors
Document Type
Comment
Metadata
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License
cc_by_nc_nd
Abstract
Keywords
Molecular Medicine, Molecular Biology, Genetics
Citation
Groen, E J N & Wadman, R I 2025, 'Safety through design : Expanding options for spinal muscular atrophy gene therapy', Molecular Therapy Methods and Clinical Development, vol. 33, no. 3, 101550. https://doi.org/10.1016/j.omtm.2025.101550