IRDiRC perspectives on the application of digital biomarkers in therapeutic development for rare diseases

Publication date

2025-04

Authors

Krishna, Rajesh
Jonker, Anneliene H.
Morel, Thomas
Sakushima, Ken
Pasmooij, A. M.G.ORCID 0000-0003-0641-3829
O'Connor, Daniel

Editors

Advisors

Supervisors

Document Type

Editorial
Open Access logo

License

cc_by_nc

Abstract

New approaches are needed to streamline clinical trials of drugs for patients with rare diseases. Digital biomarkers offer one such approach, but several challenges must be addressed to realize their potential.

Keywords

Taverne

Citation

Krishna, R, Jonker, A H, Morel, T, Sakushima, K, Pasmooij, A M G & O'Connor, D 2025, 'IRDiRC perspectives on the application of digital biomarkers in therapeutic development for rare diseases', Nature Reviews Drug Discovery, vol. 24, no. 4, pp. 233-234. https://doi.org/10.1038/d41573-024-00196-z